Breaking Gene Therapy News
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3 ISCT Leaders Recognized as Global Cell and Gene Therapy Influencers - PRNewswire
Apr 24, 2019 | 11:00 am3 ISCT Leaders Recognized as Global Cell and Gene Therapy Influencers PRNewswireVANCOUVER, British Columbia, April 24, 2019 /PRNewswire/ -- Every year, The Medicine Maker, a leading, global publication in cell and gene therapy, lists the ...
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Doctors use HIV in gene therapy to fix 'bubble boy' disease - Journal Record
Apr 23, 2019 | 22:21 pmDoctors use HIV in gene therapy to fix 'bubble boy' disease Journal RecordThey were born without a working germ-fighting system, every infection a threat to their lives. Now eight babies with "bubble boy disease" have had it fixed by.
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St. Jude prepares to launch global hemophilia gene therapy trial - Memphis Business Journal
Apr 23, 2019 | 21:41 pmSt. Jude prepares to launch global hemophilia gene therapy trial Memphis Business JournalSt. Jude is trying to establish a gene therapy program to bring next-level treatment options to patients in under-resourced countries.
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Drug Regulators Look for Common Course on Gene-Therapy Reviews - Bloomberg Law
Apr 23, 2019 | 18:40 pmDrug Regulators Look for Common Course on Gene-Therapy Reviews Bloomberg LawEurope's medicines regulator is talking with its U.S. counterpart to harmonize the way the two agencies assess a new generation of therapies that repair genetic ...
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This New Technology is Making AAV Gene Therapy a Reality - SelectScience
Apr 23, 2019 | 16:55 pmThis New Technology is Making AAV Gene Therapy a Reality SelectScienceNew 'Dissolvable Microcarriers' are addressing challenges associated with AAV-based gene therapies entering the clinic.
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Novartis Says Baby's Death May Be Tied to Gene Therapy - Bloomberg
Apr 23, 2019 | 08:50 amNovartis Says Baby's Death May Be Tied to Gene Therapy BloombergNovartis AG said the death of a six-month-old baby in a study evaluating its experimental gene therapy Zolgensma was considered by the clinical trial ...
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Gene Therapy - ALS News Today
Apr 22, 2019 | 03:27 amGene Therapy ALS News TodayGene therapy uses different approaches to modify specific genes within a cell to rectify the damage caused by mutated genes known to cause ALS.
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Mustang Bio soars after its novel gene therapy cured ‘Bubble Boys’ - The Seattle Times
Apr 22, 2019 | 02:00 amMustang Bio soars after its novel gene therapy cured ‘Bubble Boys’ The Seattle TimesShares of the tiny biotechnology company Mustang Bio shot up last week following a scientific breakthrough that cured eight infants suffering from the ...
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Novartis' star gene therapy faces potential safety issue following a recent infant death in study - Endpoints News
Apr 20, 2019 | 17:12 pmNovartis' star gene therapy faces potential safety issue following a recent infant death in study Endpoints NewsNovartis got some more upbeat press earlier in the week when researchers on the Zolgensma gene therapy program outlined some updated biomarker data on ...
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Second death in Novartis gene therapy trials under investigation - Reuters
Apr 20, 2019 | 02:29 amSecond death in Novartis gene therapy trials under investigation ReutersNovartis AG, which this week announced positive interim trial results for its experimental gene therapy for spinal muscular atrophy, on Friday said investigation is ...
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Gene Therapy Cures Babies with "Bubble Boy" Disease - Genetic Engineering & Biotechnology News
Apr 19, 2019 | 11:00 amGene Therapy Cures Babies with "Bubble Boy" Disease Genetic Engineering & Biotechnology NewsEight infants with X-linked severe combined immunodeficiency (X-SCID) have been cured through an experimental gene therapy.
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'Bubble boy' gene therapy results shoot Mustang Bio's stock up 200% - BioPharma Dive
Apr 18, 2019 | 19:50 pm'Bubble boy' gene therapy results shoot Mustang Bio's stock up 200% BioPharma DiveShares in Mustang Bio soared by as much as 200% Thursday after an experimental gene therapy it holds an exclusive license to proved successful in treating ...
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Two gene therapy approvals headline CBER's FY 2018 report - Endpoints News
Apr 18, 2019 | 15:53 pmTwo gene therapy approvals headline CBER's FY 2018 report Endpoints NewsThe FDA Center for Biologics Evaluation and Research (CBER) on Wednesday published its fiscal year 2018 report, highlighting two gene therapy approvals, ...
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'Bubble Boy' Disease Helped By Advances In Gene Therapy : Shots - Health News - NPR
Apr 17, 2019 | 23:12 pm'Bubble Boy' Disease Helped By Advances In Gene Therapy : Shots - Health News NPRThe latest advance is not only encouraging news for patients with severe combined immunodeficiency. It's a test case for all those scientists working to develop ...
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Conservative thinkers urge caution on gene therapy - Politico
Apr 16, 2019 | 18:00 pmConservative thinkers urge caution on gene therapy PoliticoSupreme Court asks for admin input on PBM case — Achaogen bankruptcy points to challenges for superbug-focused companies.
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Dystrogen Therapeutics’ Gene Therapy Shows Promise for Huntington’s - Huntington's Disease News
Apr 16, 2019 | 09:00 amDystrogen Therapeutics’ Gene Therapy Shows Promise for Huntington’s Huntington's Disease NewsDYST 201, a gene therapy targeting only the mutated forms of the Huntington's disease gene, shows promising results, Dystrogen Therapeutics announced.
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Catalent to acquire gene therapy service firm Paragon - Chemical & Engineering News
Apr 15, 2019 | 23:56 pmCatalent to acquire gene therapy service firm Paragon Chemical & Engineering NewsInvestment in gene therapy capacity has exploded. April 2019. Catalent agrees to pay $1.2 billion for Paragon Bioservices. March 2019. Thermo Fisher buys ...
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Catalent to buy Paragon for $1.2B as gene therapy demand grows - BioPharma Dive
Apr 15, 2019 | 18:08 pmCatalent to buy Paragon for $1.2B as gene therapy demand grows BioPharma DiveCatalent is making a bid to strengthen its position as a contracted developer and manufacturer of gene therapies by acquiring Paragon Bioservices for $1.2 ...
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Gene Therapy Was Hailed as a Revolution. Then Came the Bill - Bloomberg
Apr 7, 2019 | 09:00 amGene Therapy Was Hailed as a Revolution. Then Came the Bill BloombergDozens of revolutionary gene therapies that mend faulty strands of DNA are on their way, bringing the power to eliminate lethal childhood diseases, rare blood ...
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CRISPR and Beyond: Advances in Gene Therapy - Genetic Engineering & Biotechnology News
Apr 2, 2019 | 09:00 amCRISPR and Beyond: Advances in Gene Therapy Genetic Engineering & Biotechnology NewsIn this supplement—CRISPR and Beyond: Advances in Gene Therapy—we delve into some of the most exciting frontiers in gene therapy, many of which involve ...
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