Breaking Gene Therapy News

The new gene therapy that could help save sight - ANU Science

Aug 22, 2019 | 03:36 am

The new gene therapy that could help save sight ANU ScienceA new gene therapy being developed at The Australian National University (ANU) will help people at risk of dry age-related macular degeneration (AMD) and ...

Pfizer injects $500M more into gene therapy manufacturing - BioPharma Dive

Aug 21, 2019 | 21:44 pm

Pfizer injects $500M more into gene therapy manufacturing BioPharma DivePfizer intends to spend $500 million expanding its gene therapy operations in North Carolina, the latest big pharma investment in the burgeoning technology.

Gene therapy could help save eyesight - The Canberra Times

Aug 21, 2019 | 20:30 pm

Gene therapy could help save eyesight The Canberra TimesA new therapy could provide hope to those at risk of dry age-related macular degeneration.

Promising gene replacement therapy moves forward - Medical Xpress

Aug 21, 2019 | 20:00 pm

Promising gene replacement therapy moves forward Medical XpressResearch led by Dr. Krystof Bankiewicz, who recently joined The Ohio State University College of Medicine, shows that gene replacement therapy for ...

FDA on Novartis data manipulation controversy: 'We happened to be lucky' - STAT

Aug 21, 2019 | 10:38 am

FDA on Novartis data manipulation controversy: 'We happened to be lucky' STATA top agency official suggested that the FDA was so distressed by the matter in part because the stakes in gene therapy research are so high.

Conference on gene therapy for HIV cures will highlight progress and challenges ahead - Fred Hutch News Service

Aug 20, 2019 | 19:20 pm

Conference on gene therapy for HIV cures will highlight progress and challenges ahead Fred Hutch News ServiceAt the 5th Conference on Cell & Gene Therapy for HIV Cure, hosted by Fred Hutch in Seattle this week, researchers will discuss progress and the challenges ...

Sarepta now needs flawless progress for gene therapy - BioPharma Dive

Aug 20, 2019 | 18:12 pm

Sarepta now needs flawless progress for gene therapy BioPharma DiveOvernight, Sarepta became more dependent on its Duchenne muscular dystrophy gene therapy project. The Food and Drug Administration on Monday rejected ...

Parkinson's Gene Therapy in Clinical Trial, AXO-Lenti-PD, Safe And Effective in Monkey Model of Disease, Study Says - Parkinson's News Today

Aug 20, 2019 | 14:00 pm

Parkinson's Gene Therapy in Clinical Trial, AXO-Lenti-PD, Safe And Effective in Monkey Model of Disease, Study Says Parkinson's News TodayThe experimental gene therapy AXO-Lenti-PD (OXB-102) was seen to be both safe and effective in a primate model of Parkinson's disease, a study reported, ...

Novartis Delayed Reveal Of Bad Data For $2.1 Million Gene Therapy. Now Patients And Pharma Suffer. - Forbes

Aug 20, 2019 | 13:52 pm

Novartis Delayed Reveal Of Bad Data For $2.1 Million Gene Therapy. Now Patients And Pharma Suffer. ForbesNarasimhan's poor decision making has had negative consequences not just for Novartis but also for the industry and patients. Let's hope it's not repeated.

Grassroots group mobilizes to help toddlers access SMA gene therapy - STAT

Aug 20, 2019 | 10:36 am

Grassroots group mobilizes to help toddlers access SMA gene therapy STATWhen the family of 20-month-old Maisie Green heard late last month that their insurance company in Grand Junction, Colo., had agreed to cover a new gene ...

Hacking Ourselves: The Promise of Gene Therapy - Interesting Engineering

Aug 17, 2019 | 08:36 am

Hacking Ourselves: The Promise of Gene Therapy Interesting EngineeringCould gene therapy be the cure-all for all present and future diseases? Let's find out.

Will Long-Term Post-Marketing Studies Become the Norm for Gene Therapy Companies? - BioSpace

Aug 16, 2019 | 17:54 pm

Will Long-Term Post-Marketing Studies Become the Norm for Gene Therapy Companies? BioSpaceCurrent rules set by the FDA allow companies to assess whether or not long-term follow-ups are required based on risk factors determined by the company.

Leaders of AveXis Out Over Doctored Gene Therapy Data - The Scientist

Aug 14, 2019 | 22:51 pm

Leaders of AveXis Out Over Doctored Gene Therapy Data The ScientistNovartis, which bought the biotech firm in 2018, announced that the company's top scientists have left, and news reports say it's because they were involved in ...

First clinical trial of drug-inducible gene therapy yields encouraging preliminary results - Medical Xpress

Aug 14, 2019 | 20:00 pm

First clinical trial of drug-inducible gene therapy yields encouraging preliminary results Medical XpressImmunotherapeutic drugs are a potent way of transforming the immune system into a ferocious guard dog that can sniff out and destroy tumor cells. But for some ...

Toddler denied $2.1m gene therapy will now get it for free - STAT

Aug 12, 2019 | 09:00 am

Toddler denied $2.1m gene therapy will now get it for free STATA 2 1/2-year-old girl deemed ineligible for the world's most expensive drug will get the $2.1 million medicine to treat her rare genetic disease after all.

Bio Roundup: Surprise News, a Gene Therapy Mess & a CAR-T Step - Xconomy

Aug 9, 2019 | 09:00 am

Bio Roundup: Surprise News, a Gene Therapy Mess & a CAR-T Step XconomyGene therapy has become one of the hottest fields in biomedicine, with two treatments approved in the US already and several more on the way. But surprise.

Medicare to Cover Breakthrough Cancer Gene Therapy - WebMD

Aug 8, 2019 | 09:00 am

Medicare to Cover Breakthrough Cancer Gene Therapy WebMDStudies have shown that CAR-T is effective against certain types of cancers, but can cause severe side effects.

Statement on data accuracy issues with recently approved gene therapy - FDA.gov

Aug 6, 2019 | 09:00 am

Statement on data accuracy issues with recently approved gene therapy FDA.govAs a public health agency, we believe that it is critical to facilitate the development of innovative safe and effective medical products, like the cellular and gene ...

Creative leadership needed for cell and gene therapy companies - STAT

Aug 2, 2019 | 09:00 am

Creative leadership needed for cell and gene therapy companies STATWhen it comes to leadership, cell and gene therapy companies are carving out unique paths. Creativity and diversity are essential for building teams.

How do you toast a gene therapy trial? With tea.| NHGRI - National Human Genome Research Institute

Jul 23, 2019 | 09:00 am

How do you toast a gene therapy trial? With tea.| NHGRI National Human Genome Research InstituteIt's teatime and doctors, researchers and patients are at the table. They celebrate a decade of work and launch the first in-human gene therapy trial for children ...

Main Menu

Login

Related Links