Gene Therapy Net Newsletter

Main Menu

Login

Newsletter December 2022

News: FDA Approves First Gene Therapy for Hemophilia B

The FDA has approved etranacogene dezaparvovec for the treatment of adults with Hemophilia B who are currently using Factor IX prophylaxis therapy, have a history of life-threatening hemorrhaging, or have serious spontaneous bleeding episodes. The adeno-associated virus vector-based therapy is the first-of-its-kind for the treatment of Hemophilia B. “Gene therapy for hemophilia has been on the horizon for more than two decades,” Peter Marks, MD, PhD, director of the FDA’s Center for Biologics Evaluation and Research, said in a press release. “Despite advancements in the treatment of hemophilia, the prevention and treatment of bleeding episodes can adversely impact individuals’ quality of life.”

Conference: Cell & Gene Therapy tracks at PepTalk 2023

The Cell & Gene Therapy pipeline at PepTalk 2023 (January 16-20, 2023) features two back-to-back conferences and a foundational training seminar on the critical challenges facing the analysis, characterization, quality control, scale-up, and manufacture of cell and gene therapies. Some of the topics to be discussed include product and process characterization, critical quality attributes, analytical toolbox, product development, process development, and scale-up, and the role of CDMOs. Save $200 off the current rate. Reference discount code GTN2023 upon registering.

Conference: RNA Cell Therapy Summit

The inaugural RNA Cell Therapy Summit (January 24 - 26, 2023) is the first of its kind to unite 80+ industry and academic pioneers from both the RNA and cell therapy field to bridge-the-gap between transient RNA engineering and cell therapy development.

Join industry trailblazers at Cartesian, Sanofi, Intellia, Editas, Capstan and more to future-proof your pipeline with the pinnacle of cell engineering to develop the next-generation of safer, more functional and scalable CTx through the clinic.

Conference: Viral Vector Process Development Summit

The inaugural Viral Vector Process Development Summit (January 31 – February 2, 2023) is premier platform tailored for Upstream and Downstream Process Development Scientists, Viral Vector Technology, CMC and Production Leads to share their lessons learned and inspirations to overcome bottlenecks. The 3-days summit, joined by the likes of Bristol Myers Squibb, Boehringer Ingelheim, Vertex, Takeda, Ultragenyx will equip you with i.e. novel strategies to optimize upstream viral vector processes with improved cell line suspension.

Conference: 14th Annual RNA Therapeutics conference 2023

In 2023 we will see the return of SAE’s 14th Annual RNA Therapeutics conference (February 8 – 9, 2023)to a live in-person event, showcasing an update on mRNA therapeutic applications, coupled with an industry outlook of the field. We will also explore the latest trends in novel RNA therapies, including developments in AI modelling and small molecule modulation of RNA. Further topics to be examined comprise of novel RNA modalities encompassing self-amplifying RNA, saRNA, circular RNA, lnc RNA and many more.
Don't miss this unmissable opportunity to network with the pharma and biotech community of global experts in the UK and Europe.

Conference: 6th Annual Cell and Gene Therapy Innovation Summit

This summit (February 15-16, 2023) is an exclusive in-person-only gathering for up to 200 decision-makers, intellectual vanguards and captains of industry. With more regenerative medicine products approaching clinical testing and commercialisation, seize this opportunity to hear detailed insights and industry best practices from renowned presenters. #CGTI 2023 programme will highlight the manufacturing challenges facing Cell & Gene Therapy, bringing clear insights and industry best practices from industry leaders. Register now and use code GeneTherapyNet for 20% discount.

Conference: 6th CAR-TCR Summit Europe

The 6th CAR-TCR Summit Europe returns to London this February 21-23, 2023 to drive the next generation of cutting-edge innovation from global CAR and TCR leaders. 50+ leading CAR-TCR drug developers will share data-driven case studies covering the hottest topics including multiplexed engineering, armouring, in vivo engineering, combination therapies, advanced trail design and automated manufacturing.
With a focus on enhancing clinical performance for early line treatment, join 300+ of your global colleagues to gain insights on 3rd, 4th and 5th generation CAR and TCR based therapies across three tracks: Novel Platforms, Advanced Clinical Development and Streamlined Manufacturing Processes.

Conference: 3rd Annual Gene Therapy for Muscular Disorders Summit

Efficiently Target & Transduce Muscle Cells to Reduce Toxicity Risk, Increase Efficacy, & Administer High Dose Systemic Genetic Therapies Safely.
The past twelve months have seen an unprecedented level of excitement, investment, and progression within the gene therapy for muscular disorders field. As the industry endeavours to move gene therapy treatment through the preclinical and clinical pipeline, in context of reducing toxicity and increasing efficacy, attending the 3rd Annual Gene Therapy for Muscular Disorders Summit (February 21-23, 2023) has never been so crucial.
This year’s summit will return to Boston to reunite 100+ leading experts in biotech, pharma and academia to continue to develop strategies to deliver safer and more effective gene therapies to muscle cells.

Conference: 11th Alzheimer’s & Parkinson’s Drug Development Summit

With a surge in preclinical investment, fresh news of clinical pipeline progressions, and a new era of therapies pending FDA approvals from Biogen, Eisai, and Denali Therapeutics, 2022 has put neurodegenerative drug development back on the map.
Building on the field’s momentum, we are delighted to bring back the 11th Alzheimer’s & Parkinson’s Drug Development Summit (February 21-23, 2023), dedicated to overcoming the translational challenges of targeting neurodegenerative mechanisms. This summit will unite neurodegenerative biopharma experts from discovery, preclinical, translational, and clinical backgrounds to showcase the latest breakthroughs in Alzheimer’s, Parkinson’s, and related neurological disorders in 2022 and 2023.

Upcoming conferences and meetings

10 - 12 January 2023 - Pre-Filled Syringes and Injectable Drug Devices Europe - London, UK
16 - 20 January 2023 - PepTalk 2023 - Cell & Gene Therapy tracks - San Diego, CA
23 - 24 January 2023 - Transdermal and Microneedle Drug Delivery - London, UK
24 - 26 January 2023 - Next Generation Ophthalmic Drug Delivery Summit - San Francisco, CA
24 - 26 January 2023 - 2nd Annual mRNA-Based Therapeutics Summit - Berlin, Germany
24 - 26 January 2023 - RNA-Enhanced Cell Therapies summit - Boston, MA
30 January - 1 February 2023 - 2nd Allogeneic Cell Therapies Summit Europe - London, UK
30 January - 1 February 2023 - 3rd TGF-β for Immuno-Oncology Drug Development Summit - San Francisco, CA
31 January - 2 February 2023 - Viral Vector Process Development Summit - Boston, MA
8 - 9 February 2023 - 14th Annual RNA Therapeutics - London, UK
15 - 16 February 2023 - 6th Annual Cell & Gene Therapy Innovation Summit - Berlin, Germany
21 - 23 February 2023 - Retinal Vascular Disease Drug Development Summit - Boston, MA
21 - 23 February 2023 - 6th CAR-TCR Summit Europe - London, UK
21 - 23 February 2023 - 11th Alzheimer’s & Parkinson’s Drug Development Summit - San Francisco, CA
21 - 23 February 2023 - 3rd Annual Gene Therapy for Muscular Disorders Summit - Boston MA
23 - 24 February 2023 - GENAP Summit 2023 - Gene & Cell Therapy Aseptic Processing Technology - Milan, Italy
27 February - 1 March 2023 - 6th Antigen-Specific Immune Tolerance Summit - Boston, MA
7 - 8 March 2023 - Cell & Gene Therapy Research & Development Congress Asia - Taipei, Taiwan
7 - 9 March 2023 - 4th Supply Chain and Logistics for Cell Therapies Summit - Boston, MA
14 - 16 March 2023 - 6th Annual Bioprocessing Summit Europe - Barcelona, Spain
20 - 22 March 2023 - 12th Spring Meeting of the International Society for BioProcess Technology - Norfolk, VA
20 - 23 March 2023 - 6th Annual Gene Therapy for Rare Disorders 2023 Summit - Boston, MA
28 - 29 March 2023 - Reuters Pharma USA 2023 - Cell and Gene Therapies - Philadelphia, PA
28 - 30 March 2023 - 8th Innate Killer Summit - San Diego, CA
17 - 19 April 2023 - Advancing Gene Therapy 2023 - Boston, MA
26 - 27 April 2023 - World Oncology Cell Therapy Congress USA - Boston, MA
8 - 10 May 2023 - ISBioTech Nucleic Acids meeting - Production of DNA and RNA Biotherapeutics - Savannah, GA
10 - 12 May 2023 - Bioprocessing Events 2023 - Berlin, Germany
17 - 20 May 2023 - American Society of Gene and Cell Therapy (ASGCT) 26th Annual Meeting - Los Angeles, CA
24 – 27 October 2023 - Annual Congress of the European Society of Gene and Cell Therapy - Brussels, Belgium

Advertise on this site?

Advertising opportunities on Gene Therapy Net include standard size banners as well as text ads. Click here for more information about advertising.

You can also make a donation by PayPal and support the Gene Therapy Net website.