News-Medical.Net Gene Therapy News
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Researchers treat TMC1-related deafness with gene therapy
Jun 4, 2020 | 07:10 amWhen Wei Hsi (Ariel) Yeh was a young undergraduate student, one of her close friends went from normal hearing to complete deafness in the span of one month.
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New technique opens the door to treating genetic forms of hearing loss
Jun 4, 2020 | 04:10 amUsing a new genetic engineering technique, known as base editing, researchers from Boston Children's Hospital and the Broad Institute of MIT and Harvard, have restored hearing in mice with a known recessive genetic mutation.
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New advance addresses a big challenge with using CRISPR in cancer patients
Jun 3, 2020 | 01:45 amA mutation unique to certain cancer tumors is a potential homing beacon for safely deploying CRISPR gene editing enzymes to disarm DNA that makes cancer cells resistant to treatment, while ignoring the gene in normal cells where it's critical to healthy function, according to a new study from ChristianaCare's Gene Editing Institute in the journal Molecular Cancer Research.
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CSL Behring and Seattle Children's partner to develop gene therapies for primary immunodeficiency diseases
Jun 2, 2020 | 23:50 pmSeattle Children's Research Institute, one of the top pediatric research institutions in the world, and global biotechnology leader CSL Behring announced a strategic alliance to develop stem cell gene therapies for primary immunodeficiency diseases.
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Microperimetry can help determine the efficacy of novel treatments for macular diseases
Jun 2, 2020 | 22:53 pmStargardt disease is an inherited eye disease. Its onset is typically in adolescence and it is among the leading causes of blindness in this age group. Symptoms range from severe loss of sharp vision to almost complete loss of sight.
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Toshiba and Shinshu University jointly develop a 'tumor-tropic liposome technology' for gene therapy
May 30, 2020 | 12:09 pmToshiba Corporation and a team led by Professor Yozo Nakazawa at the Department of Pediatrics, Shinshu University, have together developed a “tumor-tropic liposome technology” for gene therapy. The technology uses unique, nano-sized biodegradable liposomes developed by Toshiba to accurately and efficiently deliver therapeutic genes to targeted cancer cells, and achieves safer gene delivery than viruses used as carriers.
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Using gene therapy to help the body to make its own cancer drugs
May 30, 2020 | 02:09 amImagine that we could instruct our bodies to make the drugs they need themselves. The gene technology that makes this possible is called mRNA therapy, which may become a major tool in the treatment of multiple diseases.
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Nanoscope received NIH grant to advance ultrafast laser-based gene delivery to the retina
May 29, 2020 | 03:57 amThe Nanoscope team has developed Multi-Characteristic Opsins to sensitize cells toward low level of white light so that vision is improved at ambient room light.
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Frog brain discovery may pave the way for repairing birth defects in humans
May 28, 2020 | 07:42 amA team of researchers from Tufts University, Universitat de Valencia, and Harvard University has discovered that the brains of developing frog embryos damaged by nicotine exposure can be repaired by using “ionoceuticals” that can help in the recovery of bioelectric patterns in the embryo.
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Researchers study how brain cancer cells acquire resistance to radiation
May 15, 2020 | 02:29 amIn a vertical climb to avoid collision with a towering mountain, a plane ejects cargo to gain altitude. Investigators at the University of Minnesota showed that cancer cells perform similar feats in escaping the killing effects of radiation.
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