New and Updated Clinical Gene Therapy Trials
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Gene Therapy Communication: Use of a Needs Assessment to Drive Decision-AIDS for Gene Therapy for Rare Diseases (GENETX)
Apr 12, 2023 | 18:00 pmCondition: Sickle Cell DiseaseIntervention: Other: InterviewSponsor: St. Jude Children's Research HospitalRecruiting
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Promising ROd-cone DYstrophy Gene therapY
Mar 1, 2023 | 18:00 pmCondition: Retinitis PigmentosaIntervention: Drug: SPVN06Sponsor: SparingVisionRecruiting
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Motixafortide and Natalizumab to Mobilize CD34+ Hematopoietic Stem Cells for Gene Therapies in Sickle Cell Disease (SCD)
Nov 16, 2022 | 18:00 pmCondition: Sickle Cell DiseaseInterventions: Drug: Motixafortide; Drug: Natalizumab; Procedure: LeukapheresisSponsors: Washington University School of Medicine; BioLineRx, Ltd.; BiogenNot yet recruiting
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Safety and Efficacy of TSHA-102 in Adult Females With Rett Syndrome (REVEAL Adult Study)
Nov 7, 2022 | 18:00 pmCondition: Rett SyndromeIntervention: Genetic: TSHA-102Sponsor: Taysha Gene Therapies, Inc.Recruiting
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Gene Therapy for Cardiomyopathy Associated With Friedreich's Ataxia
Jul 6, 2022 | 18:00 pmConditions: Friedreich Ataxia; Cardiomyopathy, SecondaryInterventions: Genetic: Low dose LX2006; Genetic: Mid Dose LX2006; Genetic: High Dose LX2006Sponsor: Lexeo TherapeuticsRecruiting
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Pivotal 2 Study of RGX-314 Gene Therapy in Participants With nAMD
Jun 7, 2022 | 18:00 pmConditions: AMD; nAMD; Wet Age-related Macular Degeneration; wAMD; WetAMD; CNVInterventions: Genetic: RGX-314 Dose 1; Genetic: RGX-314 Dose 2; Biological: Aflibercept (EYLEA®)Sponsor: AbbVieRecruiting
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Gene Therapy for Chinese Hemophilia A
Jan 28, 2021 | 18:00 pmConditions: Hemophilia A; Gene TherapyIntervention: Genetic: Injection of GS001Sponsor: Institute of Hematology & Blood Diseases HospitalRecruiting
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Lentiviral Gene Therapy for Epilepsy
Oct 26, 2020 | 17:00 pmCondition: Drug Resistant EpilepsyIntervention: Genetic: lentiviral gene therapySponsors: University College, London; Medical Research CouncilNot yet recruiting
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A Study to Evaluate the Efficacy and Safety of Factor IX Gene Therapy With PF-06838435 in Adult Males With Moderately Severe to Severe Hemophilia B
Mar 4, 2019 | 18:00 pmCondition: Hemophilia BIntervention: Biological: PF-06838435/ fidanacogene elaparvovecSponsor: PfizerRecruiting
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Follow-Up Study of Subjects Previously Enrolled in Poxviral Vector Gene Transfer Studies
Mar 22, 2007 | 17:00 pmConditions: Prostate Cancer; Liver Cancer; Breast Cancer; Colon Cancer; Lung CancerIntervention: Sponsor: National Cancer Institute (NCI)Recruiting
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