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New and Updated Clinical Gene Therapy Trials
Gene therapy studies updated or received in the last 30 days at ClinicalTrials.gov. Only open studies, recruiting or not yet recruiting, are shown found by a search using the keyword: "gene therapy OR gene transfer OR virus delivery"
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Gene Therapy Communication: Use of a Needs Assessment to Drive Decision-AIDS for Gene Therapy for Rare Diseases (GENETX)
12 April 2023Condition: Sickle Cell DiseaseIntervention: Other: InterviewSponsor: St. Jude Children's Research HospitalRecruiting
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Study of Gene Therapy Using a Lentiviral Vector to Treat X-linked Chronic Granulomatous Disease
09 September 2014Condition: Granulomatous Disease, Chronic, X-linkedIntervention: Biological: Lentiviral G1XCGD Gene TherapySponsors: University of California, Los Angeles; Boston Children's Hospital; National Heart, Lung, and Blood Institute (NHLBI); Genethon; California Institute for Regenerative Medicine (CIRM)Recruiting
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Liver Biopsy Following Gene Therapy For Hemophilia
06 July 2023Conditions: Hemophilia A; Hemophilia BIntervention: Procedure: Liver BiopsySponsor: St. Jude Children's Research HospitalNot yet recruiting
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Follow-Up Study of Subjects Previously Enrolled in Poxviral Vector Gene Transfer Studies
22 March 2007Conditions: Prostate Cancer; Liver Cancer; Breast Cancer; Colon Cancer; Lung CancerIntervention: Sponsor: National Cancer Institute (NCI)Recruiting
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Gene Therapy for Hemophilia B Patients Aged 12-18 Years Old
02 February 2023Condition: Hemophilia BIntervention: Drug: BBM-H901Sponsor: Institute of Hematology & Blood Diseases Hospital, ChinaRecruiting
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AFFINITY DUCHENNE: RGX-202 Gene Therapy in Participants With Duchenne Muscular Dystrophy (DMD)
20 January 2023Condition: Duchenne Muscular DystrophyIntervention: Genetic: RGX-202Sponsor: REGENXBIO Inc.Recruiting
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Safety, Tolerability, and Efficacy Study of Intrathecally Administered Gene Therapy AMT-162 in Amyotrophic Lateral Sclerosis (ALS) Patients With SOD1 Mutations
25 October 2023Condition: Amyotrophic Lateral SclerosisIntervention: Drug: AMT-162Sponsor: UniQure Biopharma B.V.Not yet recruiting
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Safety and Efficacy of TSHA-102 in Pediatric Females With Rett Syndrome (REVEAL Pediatric Study)
30 November 2023Condition: Rett SyndromeIntervention: Genetic: TSHA-102Sponsor: Taysha Gene Therapies, Inc.Not yet recruiting
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Safety and Efficacy of TSHA-102 in Adult Females With Rett Syndrome (REVEAL Adult Study)
07 November 2022Condition: Rett SyndromeIntervention: Genetic: TSHA-102Sponsor: Taysha Gene Therapies, Inc.Recruiting
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Long-Term Follow-up of Gene Therapy for APOE4 Homozygote Alzheimer's Disease
01 June 2022Condition: Alzheimer DiseaseIntervention: Biological: LX1001Sponsor: Lexeo TherapeuticsRecruiting
Clinical Trial Information
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Info ClinicalTrials.gov
Clinical gene therapy trials recently received at ClinicalTrials.gov database.
The U.S. National Institutes of Health, through its National Library of Medicine, has developed ClinicalTrials.gov to provide patients, family members and members of the public current information about clinical research studies. The database is a registry of federally and privately supported clinical trials conducted in the United States and around the world. ClinicalTrials.gov gives you information about a trial's purpose, who may participate, locations, and phone numbers for more details.
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Latest clinical trials |
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Search clinical trials |
The U.S. National Institutes of Health, through its National Library of Medicine, has developed ClinicalTrials.gov to provide patients, family members and members of the public current information about clinical research studies. The database is a registry of federally and privately supported clinical trials conducted in the United States and around the world. ClinicalTrials.gov gives you information about a trial's purpose, who may participate, locations, and phone numbers for more details.
Participate in Trial
Are you a patient and considering to participate in a clinical gene therapy trial? Your doctor may be an excellent resource to help identify clinical trials for a particular disease. There are a number of online resources that can also assist in locating clinical trials that are accepting patients:
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ClinicalTrials.gov |
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Cancer.gov |
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CenterWatch |
When looking for a clinical trial, remember to make sure the trial is appropriate for the disease. Most trials also specify an age range for the participants. Additional eligibility requirements must also be met, but these will vary depending on the individual study. Contact the health professionals if they are not listed. It is always best to discuss these issues before you travel to gene therapy center. More clinical trial information.
Be aware that Gene Therapy Net is not intended to replace or constitute the giving of medical treatments or advice.