Special News Items

• Bluebird bio’s Skysona led to seven cases of blood cancer in gene therapy trials
• ISCT Becomes the First Cell and Gene Therapy Organization to Achieve ANAB Accreditation for Workforce Development
• First patient dosed in uniQure trial of AMT-191 gene therapy for Fabry
• Researchers say gene therapy breakthrough shows promise for glaucoma
• Switching Gene Therapy On and Off with a Pill
• Toddler Born Deaf Can Hear After Gene Therapy Trial Breakthrough Her Parents Call "Mind-Blowing"
• First Patient Begins Newly Approved Sickle Cell Gene Therapy
• FDA approves Orchard’s Lenmeldy gene therapy for MLD
• Team performs the first gene therapy tests in a whole human liver
• Gene Therapy Success in Hereditary Angioedema Patients
• FDA Approves CRISPR Gene Therapy to Treat Blood Disorder
• FDA Signals Imminent Approval for Sarepta’s Duchenne Gene Therapy: A Major Breakthrough for Patients
• Revolutionary gene therapy shows promise in treating autism
• Cell & Gene Therapy Space Gears Up for First CRISPR Approval
• Gene therapy restores hearing in children with rare form of deafness
• UK biotech AlveoGene launches with plans for inhaled gene therapy
• Gene Therapy Targets Chronic Pain
• Gene therapy eyedrops restored a boy's sight. Similar treatments could help millions
• Gene therapy approved by FDA for certain boys with rare genetic condition
• FDA Needs More Cell, Gene Therapy Mid Managers to Speed Reviews
• Biology Professor Venigalla Rao Makes Breakthrough on Gene Therapy Research
• Multisystemic Smooth Muscle Dysfunction Syndrome (MSMDS)
• Bacterial ‘Nanosyringe’ Could Deliver Gene Therapy to Human Cells
• EU approves Hemgenix, one-time gene therapy for hemophilia B
• FDA officials offer advice on gene therapy trials
• New gene therapy delivers treatment directly to brain
• FDA approves Ferring’s Adstiladrin as first gene therapy for bladder cancer
• FDA Approves First Gene Therapy for Hemophilia B
• FDA finalizes neurodegenerative disease gene therapy guidance
• Gene Therapy Rapidly Improves Night Vision in Adults with Congenital Blindness