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Researchers identify new gene variants that may cause inherited retinal dystrophies
Oct 20, 2021 | 07:45 amAn international team of researchers, led by scientists at University of California San Diego and Shiley Eye Institute at UC San Diego Health, has broadened and deepened understanding of how inherited retinal dystrophies (IRDs) affect different populations of people and, in the process, have identified new gene variants that may cause the diseases.
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New technology streamlines the development of gene therapy for genetic blinding disorders
Oct 20, 2021 | 05:05 amA novel computational platform developed by researchers from the University of Pittsburgh School of Medicine identifies top-performing viral vectors that could deliver gene therapies to the retina with maximum efficiency and precision.
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Researchers reveal the mechanism of artificial chromosome formation in C. elegans' embryos
Oct 19, 2021 | 04:45 amA research team led by Dr Karen Wing Yee YUEN, Associate Professor from the School of Biological Sciences at the University of Hong Kong (HKU), revealed the mechanism of artificial chromosome (AC) formation in the embryos of the model organism Caenorhabditis elegans, a 1-mm long, transparent nematode.
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Researchers report long-lasting effects of gene therapy in children with deadly immune disorder
Oct 18, 2021 | 08:45 amOver a decade ago, UCLA physician-scientists began using a pioneering gene therapy they developed to treat children born with a rare and deadly immune system disorder.
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Devastating genetic disease in children may be treatable in adulthood
Oct 16, 2021 | 03:31 amA devastating genetic disease called CDKL5 deficiency disorder (CDD), which strikes in early childhood, may be significantly treatable even in adulthood, a new study from the Perelman School of Medicine at the University of Pennsylvania suggests.
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Researchers identify neurons and signaling pathways that make sexually receptive females more active
Oct 15, 2021 | 07:14 amScientists have known for a century that female animals become more active just as they are about to ovulate, a behavior that evolved to enhance their chances of mating when they are fertile.
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Developing New Technology for the Encapsulation of mRNA-Based Vaccines in Lipid Nanoparticles (LNPs)
Oct 14, 2021 | 10:34 amNewsMed speaks to KNAUER about the company’s background, its range of specialisms and its pioneering work to facilitate the largescale production of LNPs while meeting the stringent regulations and exacting demands of the biopharmaceutical industry.
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Drug developed at Duke is approved by FDA as only therapy for congenital athymia
Oct 12, 2021 | 03:12 amThe phone rang into the pediatric unit that Louise Markert, M.D., Ph.D., was staffing as a junior faculty member in 1991. Had she not answered, there would have been little hope for the more than one hundred patients who were subsequently treated.
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Study supports efficacy and safety of lung-selective nanotherapy against SARS-CoV-2 infection
Oct 8, 2021 | 15:50 pmA new preprint shows the potential role of a host protease cathepsin L inhibitor, which mediates viral entry into the host cell by its effect on the viral spike protein.
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Australian researchers hope to switch on sight with new gene therapy
Oct 7, 2021 | 09:15 amAustralian researchers are developing a new gene therapy which they hope will ‘switch on sight’ by regenerating light-sensing photoreceptor cells in the retina at the back of the eye.
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