News-Medical.Net Gene Therapy News
-
New editorial published following adverse events of gene therapy clinical trial
Jul 3, 2020 | 07:58 amThe Editor-in-Chief of Human Gene Therapy, the first journal devoted to the field of gene therapy, and one of the world's leading experts on gene therapy have co-authored a new editorial, Moving Forward After Two Deaths in a Gene Therapy Trial of Myotubular Myopathy, in response to the news of two deaths in a now-halted gene therapy clinical trial.
Read more... -
New model helps study human hippocampal neurons
Jun 29, 2020 | 15:18 pmNeuroscientists and stem cell researchers at Lund University in Sweden have developed a research model that allows studying human hippocampal neurons, the brain cells primarily affected by Alzheimer's disease pathology.
Read more... -
Entos Pharmaceuticals selects two lead DNA vaccine candidates for COVID-19
Jun 26, 2020 | 04:49 amEntos Pharmaceuticals, a healthcare biotechnology company developing nucleic acid medicines with its Fusogenix drug delivery platform, today announced the selection of two lead candidates for a pan-coronavirus Fusogenix DNA vaccine from its prototyping program launched at the onset of the global COVID-19 pandemic.
Read more... -
Organoids can help provide new level of accuracy in prescribing anti-cancer therapies
Jun 23, 2020 | 04:11 amPrecision medicine, using the power of the human genome to diagnose and treat patients, is about to get even more precise.
Read more... -
Synthetic peptide could be an effective COVID-19 treatment and SARS-CoV-2 vaccine
Jun 22, 2020 | 07:46 amLigandal, one of the world’s leading genetic medicine companies, has modeled a synthetic peptide that could be an effective COVID-19 treatment and SARS-CoV-2 vaccine.
Read more... -
USC researchers unlock fatal vulnerability in many cancer cells
Jun 18, 2020 | 02:09 amLike any cells in the body, cancer cells need sugar - namely glucose - to fuel cell proliferation and growth.
Read more... -
Researchers develop a simple tool for making mouse models of COVID-19
Jun 17, 2020 | 03:02 amUntil there are effective treatments or vaccines, the COVID-19 pandemic will remain a significant threat to public health and economies around the world. A major hurdle to developing and testing new anti-viral therapies and vaccines for COVID-19 is the lack of good, widely available animal models of the disease.
Read more... -
Exercise has profound protective effect in mouse models of Friedreich's ataxia
Jun 17, 2020 | 00:46 amA top exercise researcher at the University of Virginia School of Medicine is urging clinical trials of exercise in patients with Friedreich's ataxia after finding that physical activity has a "profound" protective effect in mouse models of the debilitating genetic disease.
Read more... -
UCLA receives nearly $14 million NIH grant to investigate immunotherapy to destroy HIV
Jun 16, 2020 | 19:35 pmUCLA researchers and colleagues have received a $13.65 million grant from the National Institutes of Health to investigate and further develop an immunotherapy known as CAR T, which uses genetically modified stem cells to target and destroy HIV.
Read more... -
Micro-dystrophin gene therapy can improve outcomes in children with Duchenne muscular dystrophy
Jun 16, 2020 | 07:45 amResearchers from Nationwide Children's Hospital have published in JAMA Neurology results from the first four patients treated in the first clinical trial of systemic delivery of micro-dystrophin gene therapy in children with Duchenne muscular dystrophy (DMD) - and initial findings suggest that the therapy can provide functional improvement that is greater than that observed under the standard of care.
Read more...